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El Ayuntamiento entrega 3.090 euros a los padres de la niña con 'Amaurosis congénita de lebe', QLT Announces Positive Interim Results From Phase 1b Study of its Oral Synthetic Retinoid Compound in Leber Congenital Amaurosis, Targeted Genetics Announces Data From First Gene Therapy Trial for Leber's Congenital Amaurosis in New England Journal of Medicine














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